#a1atd

❓ Did you know that the last day of February is National Rare Disease Day?

❓ Did you know that 1/10 Americans lives with a rare disease?

🔗 Head to rarediseases.org to learn more

📢 Representation in arts & media is crucial for raising awareness! So, we've curated a list of fiction books that tackle just some of the conditions considered rare diseases.

💬 There are 88 books included in this list- how many have you read?

💬 Is there a rare disease you wish had some representation in the fiction world?

ADVANCE announced the first Phase 1/2 clinical trial of ADVM-043 for A1ATD. The clinical trial is designed to evaluate the safety and protein expression following a single administration of ADVM-043, their new gene therapy candidate.